Current Research Projects
Optimized Production and Validation of Rationally Designed AAV Vectors for Cockayne Syndrome Gene Therapy
Role: Co-Primary Investigator
Funded by: United Stated Food & Drug Administration (FDA)
Start Date: September 1, 2021
End Date: August 31, 2024
Mechanisms and Treatment of Cardiac and Skeletal Muscular Dysfunction in Barth Syndrome
Funded by: National Institutes of Health - National Heart, Lung, and Blood Institute (NIH/NHLBI)
Project Start Date: July 1, 2018
Renewal Start Date: February 6, 2021
End Date: April 30, 2023
Completed Projects
Development of HITI CRISPR Gene Therapy for Dilated Cardiomyopathy in a Canine Model
Start Date: February 1, 2022
End Date: August 31, 2022